This is one of the 85 patients who suffer from this condition. The treatment for haemophilia has advanced considerably in recent decades. So the patients have the chance to live a decent life. If before there were blood transfusions, now they are a thing of the past. The newest treatment is the one with recombinant […]

Haemophylia A is 6 times more frequent than haemophilia B. However, no one expected that the gene therapy for haemophyllia A would prove effective so quickly, because the size of the viral capside (the protein coating in which the DNA is found) did not match those of the factor VIII gene, which has 7 kilobases, […]

In a study recently published in the New England Journal of Medicine, 10 men who received gene therapy for haemophilia B now produce the IX factor within normal limits. Hemorrhagic episodes have been reduced from one per month to less than one per year. The biotech company Spark developed the therapy and carried out the […]

Gene therapy means a technique of introducing a nucleic acid (DNA, RNA) into a patient’s cells for the purpose of treating certain diseases. There are methods that use viral vectors (biological nano particles), i.e. modified viruses and non-viral methods based on DNA complexes (naked DNA). When a virus infects an organism, it introduces its genetic […]

“Haemophilliawill be cured by the year 2000”–the statement of the World Health Organization in March 1994. 23 years later we can finally say that we are closer than ever to healing haemophilia through gene therapies. Tworecent studies published in the New England Journal of Medicine announce a revolution in the treatment of haemophilia A and […]